13.10.07 PCOS
Definition
Anovulation
Resulting in irregular menstruation, amenorrhea, ovulation-related infertility
Androgen excess
Resulting in acne and hirsutism
Insulin resistance
Often associated with obesity, Type 2 diabetes, and high cholesterol levels
Risk factors
FHx (autosomal dominant)
Obesity
Epilepsy
Use of anti-seizure medications
Differential diagnosis
Ovarian hyperthecosis
Congenital adrenal hyperplasia (late-onset)
Drugs (eg, danazol, androgenic progestins)
Hypothyroidism
Patients with menstrual disturbances and signs of hyperandrogenism
Idiopathic hirsutism
Familial hirsutism
Masculinizing tumors of the adrenal gland or ovary (rapid onset of signs of virilization)
Cushing syndrome
Hyperprolactinemia
Exogenous anabolic steroid use
Stromal hyperthecosis (valproic acid)
3-Beta-Hydroxysteroid Dehydrogenase Deficiency
Acromegaly
Amenorrhea
Ovarian Tumors
Epidemiology
One of the most common endocrine disorders of reproductive-age women, with a prevalence of 4-12%
A great deal of ethnic variability in hirsutism is observed
Asian (East and Southeast Asia) women have less hirsutism than white women given the same serum androgen values
PCOS affects premenopausal women, and the age of onset is most often perimenarchal (before bone age reaches 16 y)
However, clinical recognition of the syndrome may be delayed
Irregular menses, hirsutism, other PCOS findings may overlap with normal physiologic maturation during the 2 years after menarche
In lean women with a genetic predisposition to PCOS, the syndrome may be unmasked when they subsequently gain weigh
Aetiology / Pathophysiology
Abnormalities in the metabolism of androgens and estrogen and in the control of androgen production
Peripheral insulin resistance and hyperinsulinemia
Secondary to a postbinding defect in insulin receptor signaling pathways
Hyperinsulinemia => Suppression of hepatic generation of sex hormone–binding globulin (SHBG) => Androgenicity
Insulin resistance in PCOS has been associated with high adiponectin levels
Proposed mechanism for anovulation and elevated androgen levels:
Excess LH secreted by the anterior pituitary
=> Stimulation of ovarian theca cells is increased
=> Increased androgen production
Decreased FSH levels => Ovarian granulosa cells cannot aromatize the androgens to oestrogens
=> Decreased estrogen levels and consequent anovulation
Growth hormone (GH) and insulin-like growth factor–1 (IGF-1) may also augment the effect on ovarian function
Hyperinsulinemia => Dyslipidemia => Elevated plasminogen activator inhibitor-1 (PAI-1) => Intravascular thrombosis
Cinical features
FHx
Menstrual disorders
Adrenal enzyme deficiencies
Hirsutism
Infertility
Obesity and metabolic syndrome
Diabetes
Menstrual abnormalities
Abnormal menstruation patterns (attributed to chronic anovulation)
Oligomennorhoea
Secondary amenorrhea
Dysfunctional uterine bleeding
Infertility
Hyperandrogenism
Excess terminal body hair in a male distribution pattern
Hair is commonly seen on the upper lip, on the chin, around the nipples, and along the linea alba of the lower abdomen
Some patients have acne and/or male-pattern hair loss (androgenic alopecia)
The modified Ferriman-Gallwey (mFG) score grades 11 body areas from 0 (no hair) to 4 (frankly virile)
A total score of 8 or more is considered abnormal for an adult white woman; a score of 44 is the most severe
Other signs of hyperandrogenism are more characteristic of hyperthecosis
E.g. clitoromegaly, increased muscle mass, voice deepening
Could also be consistent with androgen-producing tumors, exogenous androgen administration, or virilizing congenital adrenal hyperplasia
Premature adrenarche
Infertility
A subset of women with PCOS is infertile
Most women with PCOS ovulate intermittently
Conception may take longer than in other women, or women with PCOS may have fewer children than they had planned
In addition, the rate of miscarriage is also higher in affected women
Obesity and metabolic syndrome
Nearly half of all women with PCOS are clinically obese
Many patients with PCOS have characteristics of metabolic syndrome
Abdominal obesity (waist circumference >35 in)
Dyslipidemia (triglyceride level >150 mg/dL, high-density lipoprotein cholesterol [HDL-C] level < 50 mg/dL)
Elevated blood pressure
Proinflammatory state characterized by an elevated C-reactive protein level
Prothrombotic state characterized by elevated plasminogen activator inhibitor-1 (PAI-1) and fibrinogen levels
Increased prevalence of coronary artery calcification and thickened carotid intima media, which may be responsible for subclinical atherosclerosis
Diabetes mellitus
Approximately 10% of women with PCOS have type 2 diabetes mellitus by 40 years of age
30-40% of women with PCOS have impaired glucose tolerance by 40 years of age
Sleep apnea
Many women with PCOS have obstructive sleep apnea syndrome (OSAS), which is an independent risk factor for cardiovascular disease
Acanthosis nigricans
Diffuse, velvety thickening and hyperpigmentation of the skin, thought to be the result of insulin resistance
May be present at the nape of the neck, axillae, area beneath the breasts, intertriginous areas, and exposed areas (eg, elbows, knuckles)
NB Acanthosis nigricans can also be a cutaneous marker of malignancy
Hypertension
Investigations
Bloods
TFTs
Prolactin
Total and free testosterone
Free androgen index
Serum hCG level
Cosyntropin stimulation test
Serum 17-hydroxyprogesterone (17-OHPG) level
Urinary free cortisol (UFC) and creatinine levels
Low-dose dexamethasone suppression test
Serum insulinlike growth factor (IGF)–1 level
Others
Androstenedione level
FSH and LH levels
GnRH stimulation testing
Glucose level
Insulin level
Lipid panel
Imaging
Ovarian ultrasonography, preferably using transvaginal approach
Pelvic CT scan or MRI to visualize the adrenals and ovaries
Management
Lifestyle changes
Diet + exercise
Comparable to or better than treatment with medication
Medical
Metformin
Combination low-dose oral contraceptive (reduce testosterone, LH, FSH)
Clomiphene citrate
Exogenous gonadotropins
Antiandrogens (spironolactone, leuprolide, finasteride) - NB Contraindicated in pregnancy
Topical eflornithine (for hirsutism)
Topical acne agents
Surgical
Laparoscopic ovarian drilling
Prognosis
Women with polycystic ovarian syndrome (PCOS) may be at increased risk for cardiovascular and cerebrovascular disease
Women with hyperandrogenism have elevated serum lipoprotein levels similar to those of men
Approximately 40% of patients with PCOS have insulin resistance that is independent of body weight
These women are at increased risk for type 2 diabetes mellitus and consequent cardiovascular complications
Patients with PCOS should be periodically reassessed for diabetes/IFG throughout their lifetime
Patients with PCOS are also at an increased risk for endometrial hyperplasia and carcinoma
Due to the chronic anovulation in PCOS leading to constant endometrial stimulation with oestrogen without progesterone
RCOG recommends induction of withdrawal bleeding with progestogens a minimum of every 3-4 months
No known association with breast or ovarian cancer has been found; thus, no additional surveillance is needed